R&D

Developing innovative therapeutics based on next-generation mRNA·LNP platform technology.

mRNA·LNP Platform Technology

🧬 mRNA Platform Stability Simulator

Comparison of RNase resistance: SML's Circular Poly A vs. Conventional Linear Poly A

SML's mRNA Platform (Circular Poly A)
CAP
5' UTR
GOI
3' UTR
POLY(A) 50
ADAPTOR
COMPLEMENTARY
Stability
99%
Circular structure blocks RNase access
VS
Widely Used mRNA Platform (Linear Poly A)
CAP
5' UTR
GOI
3' UTR
POLY(A) 50
AAAAAAAAAAAAAAAAAAAAAAAAAAAAAAA
Stability
100%
Exposed 3' end vulnerable to RNase degradation

An innovative mRNA overcoming conventional mRNA limitations

Higher expression levels

Achieves higher expression rates both in vitro and in vivo, enabling greater protein production with lower mRNA quantities.

Enhanced stability

Improved in vivo stability prolongs mRNA persistence in the body, partially addressing its inherent rapid degradation.

Optimized delivery

Proprietary LNP formulation ensures efficient intracellular delivery, maximizing therapeutic efficacy across diverse applications.

SML Biopharm possesses an mRNA platform with optimized UTR and poly(A) tail designed to enhance stability and expression efficiency. While advancing our next-generation mRNA platform and drug pipeline, we independently develop lipid nanoparticles (LNP) for efficient delivery, driving effective R&D and rapid research progress.

Immunotherapy

면역치료

mRNA를 통해 특정 항원을 발현시켜 면역 반응을 유도하고 치료합니다. 예방 백신과 암백신을 포함한 다양한 신약 개발이 가능합니다.

mRNA를 통한 특정 항원 발현으로 면역반응 유도 및 치료
예방 백신 및 암백신을 포함한 다양한 신약 개발 가능

In vivo Protein Therapeutics

질병 치료를 위해 특정 펩타이드나 단백질(항체, 효소 등)을 발현시킵니다. 목표 단백질 생산이 훨씬 간단하고 효율적이며, 감염병, 암, 유전 질환, 희귀 질환 등 다양한 질환에 적용할 수 있습니다.

질병 치료를 위한 특정 펩타이드/단백질 발현 (항체, 효소 등)
목표 단백질 생산이 훨씬 간단하고 효율적
감염병, 암, 유전 질환, 희귀 질환 등 다양한 질환에 적용 가능
In vivo 단백질 치료제

Pipeline

Developing innovative therapeutics for various diseases based on mRNA platform technology.

SBP-101

Cancer Vaccine

Immune Response Based Therapeutics

INDICATION Cervical Cancer
Preclinical
Screening
POC
Candidate
Optimization
Preclinical
Clinical
Ph 1
Ph 2
Ph 3
PARTNERS
SBP-102

Cancer Vaccine / mRNA-based bsAb

Immune Response Based Therapeutics

INDICATION HNSCC
POC
Screening
POC
Candidate
Optimization
Preclinical
Clinical
Ph 1
Ph 2
Ph 3
PARTNERS
SBP-801 Gov Grants

Prophylactic Vaccine

Immune Response Based Therapeutics

INDICATION COVID-19
Preclinical
Screening
POC
Candidate
Optimization
Preclinical
Clinical
Ph 1
Ph 2
Ph 3
PARTNERS
KDCA
EuBiologics
SBP-301 Gov Grants

Antibody

In-vivo Protein Expression Therapeutics

INDICATION SFTS (Severe Fever with Thrombocytopenia Syndrome)
Preclinical
Screening
POC
Candidate
Optimization
Preclinical
Clinical
Ph 1
Ph 2
Ph 3
PARTNERS
KDCA
SBP-302

mRNA-based Protein (Novel Target)

In-vivo Protein Expression Therapeutics

INDICATION Sarcopenia
POC
Screening
POC
Candidate
Optimization
Preclinical
Clinical
Ph 1
Ph 2
Ph 3
PARTNERS
SBP-303

mRNA-based bsAb

In-vivo Protein Expression Therapeutics

INDICATION Solid Cancer
POC
Screening
POC
Candidate
Optimization
Preclinical
Clinical
Ph 1
Ph 2
Ph 3
PARTNERS

Development Process

SML Biopharm's drug development process

Discovery

Target discovery and
candidate exploration

Preclinical

Preclinical testing and
efficacy/safety validation

Clinical Trial

Clinical trials
(Phase 1-3)

Regulatory

Regulatory submission
and approval

Commercialization

Commercialization and
market launch

Patents

SML Biopharm's patent portfolio

patent

Core LNP Composition Technology for mRNA Vaccines

Technology transfer from MFDS

conference

Development of Therapeutic Antibodies In Vivo

4th mRNA-Based Therapeutics Summit Europe, Germany

technology

SFTS Virus Neutralizing Antibody Sequence

License acquired from AI BIO (Developed by Prof. Jun-Ho Jung, SNU)

publication

Development of SFTS Therapeutics Using mRNA-LNP Platform

Journal of Virology, 2024

patent

mRNA Construct Comprising Optimized UTR Sequences

Korea Patent Application

Partnership Inquiry

If you are interested in R&D collaboration, please contact us.